International Fabry Congress MPS Lysosomales Association Spain
Charlotte2022-06-28T13:57:00+02:00International Fabry Congress MPS Lysosomales Association Spain
Focus on Fabry Leaders around the world
Charlotte2022-04-04T11:16:26+02:00Interview with Alejandra Tornero from Alianza Lisosomal Argentina When did you join your national patient association? I am the founder of Alianza Lisosomal Argentina – ALA – and I lead the Alliance for Patients with Fabry, Gaucher and Pompe diseases. What was the reason for joining? The reason I joined is [...]
Help us to train Face2Gene to diagnose Fabry patients earlier!
Charlotte2022-03-31T13:31:22+02:00Help us to train Face2Gene to diagnose Fabry patients earlier!
Rare Disease Day 2022
Charlotte2022-03-16T15:45:13+01:00On Rare Disease Day, the community joined together across borders and across diseases to show that; Rare is many. Rare is strong. Rare is proud! Here are some of the amazing activities our members organised!
News from Sangamo Therapeutics
Charlotte2022-02-08T16:29:44+01:00Sangamo Therapeutics Announces Updated Preliminary Phase 1/2 Data Showing Tolerability and Sustained Elevated α-Gal A Enzyme Activity in Patients With Fabry Disease
Webinar Fabry Highlights of the WorldSymposium 2023
Charlotte2023-04-07T16:01:37+02:00Join us for the Fabry Highlights from the Worldsymposium Webinar with Dr Hopkin April 5th, 2023 at 6.30pm-7.30pm CET
Fabry Expert Meeting 2022 – Virtual on May 7th
Charlotte2022-03-11T10:42:28+01:00Virtual Fabry Expert Meeting 2022 on May 7th
Addressing the Challenges of Persons Living with a Rare Disease
Charlotte2022-02-08T16:39:01+01:00Addressing the Challenges of Persons Living with a Rare Disease
Gene Therapy Approaches for Fabry Diseases
Charlotte2022-02-08T16:39:13+01:00We're are happy to share this great resource with you. This can support you in exploring different gene therapies approaches to treating Fabry disease! Have a look at the infographic to find out more!