About Charlotte

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So far Charlotte has created 39 blog entries.

News from Freeline


Freeline will be progressing to the second dose cohort in the MARVEL-1 study immediately with first patient dosing expected in mid-2022

News from Freeline2022-04-13T15:50:45+02:00

Fabry Awareness Month 2022


April 1st marks the start of Fabry Awareness Month. This year we focus our efforts on helping parents recognise Fabry symptoms in their children, with our campaign 'Cool Down Fabry'

Fabry Awareness Month 20222022-03-31T13:25:12+02:00

Focus on Fabry Leaders around the world


Interview with Alejandra Tornero from Alianza Lisosomal Argentina When did you join your national patient association? I am the founder of Alianza Lisosomal Argentina – ALA – and I lead the Alliance for Patients with Fabry, Gaucher and Pompe diseases. What was the reason for joining? The reason I joined is [...]

Focus on Fabry Leaders around the world2022-04-04T11:16:26+02:00

News from Sangamo Therapeutics


Sangamo Therapeutics Announces Updated Preliminary Phase 1/2 Data Showing Tolerability and Sustained Elevated α-Gal A Enzyme Activity in Patients With Fabry Disease

News from Sangamo Therapeutics2022-02-08T16:29:44+01:00
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