News from Freeline
Charlotte2022-04-13T15:50:45+02:00Freeline will be progressing to the second dose cohort in the MARVEL-1 study immediately with first patient dosing expected in mid-2022
Fabry Awareness Month 2022
Charlotte2022-03-31T13:25:12+02:00April 1st marks the start of Fabry Awareness Month. This year we focus our efforts on helping parents recognise Fabry symptoms in their children, with our campaign 'Cool Down Fabry'
Focus on Fabry Leaders around the world
Charlotte2022-04-04T11:16:26+02:00Interview with Alejandra Tornero from Alianza Lisosomal Argentina When did you join your national patient association? I am the founder of Alianza Lisosomal Argentina – ALA – and I lead the Alliance for Patients with Fabry, Gaucher and Pompe diseases. What was the reason for joining? The reason I joined is [...]
Help us to train Face2Gene to diagnose Fabry patients earlier!
Charlotte2022-03-31T13:31:22+02:00Help us to train Face2Gene to diagnose Fabry patients earlier!
Rare Disease Day 2022
Charlotte2022-03-16T15:45:13+01:00On Rare Disease Day, the community joined together across borders and across diseases to show that; Rare is many. Rare is strong. Rare is proud! Here are some of the amazing activities our members organised!
FIN Fabry Expert Meeting 2022 – May 7th
Charlotte2022-03-11T10:35:19+01:00Registration now open - Virtual FIN Fabry Expert Meeting 2022 on May 7th
News from Sangamo Therapeutics
Charlotte2022-02-08T16:29:44+01:00Sangamo Therapeutics Announces Updated Preliminary Phase 1/2 Data Showing Tolerability and Sustained Elevated α-Gal A Enzyme Activity in Patients With Fabry Disease
Highlights of the WorldSymposium 2022
Charlotte2022-03-11T10:42:18+01:00Fabry Highlights from the Worldsymposium Webinar with Dr Hopkin Feb 28Th at 6pm CET
Fabry Expert Meeting 2022 – Virtual on May 7th
Charlotte2022-03-11T10:42:28+01:00Virtual Fabry Expert Meeting 2022 on May 7th