About Charlotte

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So far Charlotte has created 39 blog entries.

News from Freeline


Freeline announced new data from its ongoing Phase 1/2 MARVEL-1 dose-finding clinical trial of FLT190 for the treatment of Fabry disease and provided updates on its pipeline programs. 

News from Freeline2021-12-13T18:27:08+01:00

News from Idorsia


Idorsia Ltd (SIX: IDIA) today announced that after the planned interim analysis of the open-label extension (OLE) of the Phase 3 MODIFY study with lucerastat for the treatment of adult patients with Fabry disease, the study will continue.

News from Idorsia2021-12-13T18:15:52+01:00

Focus on Fabry Leaders around the world


Interview with Yifan Xu from Fabry China  When did you join your national patient association? I joined Fabry China in 2016. At that time the community was only founded since a few months. There were only 10 members. You could hardly say it was an organization, actually more like just a [...]

Focus on Fabry Leaders around the world2021-12-20T14:03:51+01:00

News from Sangamo Therapeutics


Sangamo Therapeutics Announces Preliminary Phase 1/2 Data Showing Tolerability and Sustained Elevated α-Gal A Enzyme Activity in Patients With Fabry Disease

News from Sangamo Therapeutics2021-11-04T17:15:33+01:00
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