Industry News

News from Freeline

2022-04-13T15:50:45+02:00

Freeline will be progressing to the second dose cohort in the MARVEL-1 study immediately with first patient dosing expected in mid-2022

News from Freeline2022-04-13T15:50:45+02:00

News from Sangamo Therapeutics

2022-02-08T16:29:44+01:00

Sangamo Therapeutics Announces Updated Preliminary Phase 1/2 Data Showing Tolerability and Sustained Elevated α-Gal A Enzyme Activity in Patients With Fabry Disease

News from Sangamo Therapeutics2022-02-08T16:29:44+01:00

News from Freeline

2021-12-13T18:27:08+01:00

Freeline announced new data from its ongoing Phase 1/2 MARVEL-1 dose-finding clinical trial of FLT190 for the treatment of Fabry disease and provided updates on its pipeline programs. 

News from Freeline2021-12-13T18:27:08+01:00

News from Idorsia

2021-12-13T18:15:52+01:00

Idorsia Ltd (SIX: IDIA) today announced that after the planned interim analysis of the open-label extension (OLE) of the Phase 3 MODIFY study with lucerastat for the treatment of adult patients with Fabry disease, the study will continue.

News from Idorsia2021-12-13T18:15:52+01:00

News from Sangamo Therapeutics

2021-11-04T17:15:33+01:00

Sangamo Therapeutics Announces Preliminary Phase 1/2 Data Showing Tolerability and Sustained Elevated α-Gal A Enzyme Activity in Patients With Fabry Disease

News from Sangamo Therapeutics2021-11-04T17:15:33+01:00

Fabry Outcome Survey- Annual Report 2020

2022-02-08T16:37:44+01:00

Throughout 2020, the COVID-19 pandemic posed many challenges for both FOS and the wider Fabry disease community. The members of the FOS Steering Committee and I would like to thank all patients and caregivers involved in the registry for their extremely valuable contributions and for their continued commitment to [...]

Fabry Outcome Survey- Annual Report 20202022-02-08T16:37:44+01:00

A new tool to capture symptoms for Fabry Disease?

2021-09-30T12:02:34+02:00

In December 2020 and March 2021, people with Fabry Disease, representing five European countries shared their perspectives on standard questionnaires often used to capture the experiences of people with Fabry Disease and the ideal profile of new tools, designed to more accurately record the Fabry Disease symptoms and impacts. [...]

A new tool to capture symptoms for Fabry Disease?2021-09-30T12:02:34+02:00
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